Help Accelerate A-T Research

As we head into 2022, research to find treatments for ataxia-telangiectasia (A-T) is moving more swiftly than ever. Please help us maintain momentum by making a year-end donation. Researchers at Boston Children’s Hospital are now treating a little girl with A-T using antisense oligonucleotide (ASO) gene therapy and will soon be expanding their testing to more children. … Read More

Large-Scale Drug Screening for A-T

Dear Friends, I hope you and your families are remaining safe as Covid continues to throw new challenges at us. While the pandemic has made funding and operating the A-T Children’s Project vastly more difficult, we’re continuing to drive forward innovative research, knowing that our kids will keep deteriorating a little bit each day until … Read More

A Biomarker to Track Brain Cell Death in A-T Kids

Hi everyone, I hope you and your families are continuing to stay safe during the pandemic. Over the past year, you’ve heard me talk a lot about testing an approach called antisense oligonucleotide (ASO) gene therapy in a little girl with   A-T. She has continued to receive regular injections, and we’re grateful that we haven’t … Read More